Long-Term Evaluation of AAV-CRISPR Genome Editing for Duchenne Muscular Dystrophy

TitleLong-Term Evaluation of AAV-CRISPR Genome Editing for Duchenne Muscular Dystrophy
Publication TypeConference Paper
Year of Publication2019
AuthorsC Nelson, Y Wu, M Gemberling, M Oliver, JD Bohning, JN Robinson-Hamm, K Bulaklak, RMC Rivera, JH Collier, A Asokan, and CA Gersbach
Conference NameMolecular Therapy
Date Published04/2019